PMID: 28327546

 

    Legend: Gene, Sites

Title : Missense mutations near the N-glycosylation site of the A2 domain lead to various intracellular trafficking defects in coagulation factor VIII

Abstract :
  1. Missense mutation is the most common mutation type in hemophilia
  2. However, the majority of missense mutations remain uncharacterized
  3. Here we characterize how hemophilia mutations near the unused N-glycosylation site of the A2 domain ( N582 ) of FVIII affect protein conformation and intracellular trafficking
  4. N582 is located in the middle of a short 310-helical turn (D580-S584), in which most amino acids have multiple hemophilia mutations
  5. All 14 missense mutations found in this 310-helix reduced secretion levels of the A2 domain and full-length FVIII
  6. Secreted mutants have decreased activities relative to WT FVIII
  7. Selected mutations also lead to partial glycosylation of N582 , suggesting that rapid folding of local conformation prevents glycosylation of this site in wild-type FVIII
  8. Protease sensitivity, stability and degradation of the A2 domain vary among mutants, and between non-glycosylated and glycosylated species of the same mutant
  9. Most of the mutants interact with the ER chaperone BiP , while only mutants with aberrant glycosylation interact with calreticulin
  10. Our results show that the short 310-helix from D580 to S584 is critical for proper biogenesis of the A2 domain and FVIII , and reveal a range of molecular mechanisms by which FVIII missense mutations lead to moderate to severe hemophilia A
Output (sent_index, trigger, protein, sugar, site):
  • 0. N-glycosylation, , -, -, domain
  • 0. N-glycosylation, , -, -, site
  • 3. N-glycosylation, , -, -, domain
  • 3. N-glycosylation, , FVIII, -, N582
  • 3. N-glycosylation, , FVIII, -, domain
  • 3. N-glycosylation, , FVIII, -, site
  • 7. glycosylation, , -, -, N582
  • 7. glycosylation, , FVIII, -, site
Output(Part-Of) (sent_index, protein, site):
  • 3. FVIII, N582
  • 3. FVIII, domain
*Output_Site_Fusion* (sent_index, protein, sugar, site):
  • 3. FVIII, -, N582
  • 7. FVIII, -, N582

 

 

Protein NCBI ID SENTENCE INDEX
WT FVIII 2157 6
FVIII 2157 3,5,7,10
calreticulin 811 9